Search Result "MPS I"

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Case Report
Bone Remodeling in an Mps-1h Girl after Hematopoietic Stem CellTransplantation along with Enzymatic Replacement Therapy

Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets

Volume: 22 Issue: 14 Year: 2022 Page: 1425-1432

Author(s): Maria Felicia Faienza

Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients

Journal: Current Pharmaceutical Biotechnology

Volume: 12 Issue: 6 Year: 2011 Page: 946-955

Author(s): Patricia I. Dickson, Agnes H. Chen

Research Article
Gene Therapy of Mucopolysaccharidosis Type I Mice: Repeated Administrations and Safety Assessment of pIDUA/Nanoemulsion Complexes

Journal: Current Gene Therapy

Volume: 21 Issue: 5 Year: 2021 Page: 464-471

Author(s): Michelle Fraga,Roselena Silvestri Schuh,Édina Poletto,Talita Giacomet de Carvalho,Raqueli Teresinha França,Camila Vieira Pinheiro,Gilherme Baldo,Roberto Giugliani,Helder Ferreira Teixeira,Ursula Matte

Chloramphenicol Enhances IDUA Activity on Fibroblasts from Mucopolysaccharidosis I Patients

Journal: Current Pharmaceutical Biotechnology

Volume: 14 Issue: 2 Year: 2013 Page: 194-198

Author(s): Fabiana Quoos Mayer,Osvaldo Alfonso Artigalas,Valeska Lizzi Lagranha,Guilherme Baldo,Ida Vanessa Schwartz,Ursula Matte,Roberto Giugliani

Research Article
Estimation of Human Oral Fraction Dose Absorbed of Simvastatin from Various Formulations using in-situ Single Pass Intestinal Perfusion Method

Journal: Drug Delivery Letters

Volume: 13 Issue: 4 Year: 2023 Page: 283-295

Author(s):

Design and Synthesis of (E)-4-(2-Phenyl-2H-chromen-3-yl)but-3-en-2-ones and Evaluation of their In Vitro Antimicrobial Activity

Journal: Letters in Organic Chemistry

Volume: 12 Issue: 5 Year: 2015 Page: 352-358

Author(s): Sabita Nayak,Subhendu Chakroborty,Sujitlal Bhakta,Pravati Panda,Seetaram Mohapatra,Sanjeet Kumar,Padan Kumar Jena,Chandrasekhar Purohit

Research Article
Synthesis and In Vitro Cytotoxic Evaluation of Novel Murrayafoline A Derived β-Amino Alcohols

Journal: Letters in Organic Chemistry

Volume: 14 Issue: 8 Year: 2017 Page: 603-611

Author(s): Luu Van Chinh,Le Duc Anh,Nguyen Thi Nga,Nguyen Thi Ha Ly,Vu Thi Ha,Tran Quoc Toan,Nguyen Manh Cuong,Tran Khac Vu

Research Article
Efficacy of a Herbal Formulation Based on Foeniculum Vulgare in Oligo/Amenorrhea: A Randomized Clinical Trial

Journal: Current Drug Discovery Technologies

Volume: 17 Issue: 1 Year: 2020 Page: 68-78

Author(s): Farnoush Falahat,Sedigheh Ayatiafin,Lida Jarahi,Roshanak Mokaberinejad,Hasan Rakhshandeh,Zohre Feyzabadi,Mandana Tavakkoli

Commentary
Croton cajucara: Patents and Nanotechnological Advances

Journal: Recent Patents on Nanotechnology

Volume: 18 Issue: 4 Year: 2024 Page: 389-394

Author(s): Laís Rocha Lima,Francisco Lopes da Silva Júnior,Daniel Dias Rufino Arcanjo

Research Article
Synthesis and In vitro and In silico Anti-inflammatory Activity of NewThiazolidinedione-quinoline Derivatives

Journal: Current Topics in Medicinal Chemistry

Volume: 24 Issue: 14 Year: 2024 Page: 1264-1277

Author(s): Sandra Elizabeth Barbosa da Silva,José Arion da Silva Moura,Jeann Fabiann Branco Júnior,Paulo André Teixeira de Moraes Gomes,Simão Kalebe Silva de Paula,Douglas Carvalho Francisco Viana,Eduardo Augusto Vasconcelos de Freitas Ramalho,João Victor de Melo Gomes,Michelly Cristiny Pereira,Maira Galdino da Rocha Pitta,Marina Galdino da Rocha Pitta

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