Search Result "Mucopolysaccharidoses"
Substrate Reduction Therapies for Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 1 Year: 2011 Page: 1860-1865
Author(s): Joanna Jakobkiewicz-Banecka, Ewa Piotrowska, Magdalena Gabig-Ciminska, Elzbieta Borysiewicz, Monika Slominska-Wojewodzka, Magdalena Narajczyk, Alicja Wegrzyn, Grzegorz Wegrzyn
Targeting Brain Disease in Mucopolysaccharidoses
Ebook: Frontiers in Nanomedicine
Volume: 2 Year: 2017
Author(s): Marika Salvalaio,Laura Rigon,Francesca DâAvanzo,Elisa Legnini,Valeria Balmaceda Valdez,Alessandra Zanetti,Rosella Tomanin
Doi: 10.2174/9781681084930117020009
Cell-and Gene-based Therapeutic Approaches for Neurological Deficits in Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 884-896
Author(s): Dao Pan
Therapies for Neurological Disease in the Mucopolysaccharidoses
Journal: Current Gene Therapy
Volume: 11 Issue: 2 Year: 2011 Page: 132-143
Author(s): Donald S. Anson, Chantelle McIntyre, Sharon Byers
Help Comes from Unexpected Places: How a Tiny Fairy and a Tropical Fish may help us Model Mucopolysaccharidoses
Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets
Volume: 24 Issue: 16 Year: 2024 Page: 11-11
Author(s):
Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Emerging Treatment Strategies
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 923-930
Author(s): J. de Ruijter, M. J. Valstar, F. A. Wijburg
Hematopoietic Stem Cell Transplant in Inherited Genetic Diseases
Ebook: Recent Advances in Molecular and Translational Medicine: Updates in Precision Medicine
Volume: 1 Year: 2021
Author(s): Usanarat Anurathapan,Suradej Hongeng
Doi: 10.2174/9789815036756121010015
Perinatal Gene Transfer to the Liver
Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2528-2541
Author(s): Tristan R. McKay, Ahad A. Rahim, Suzanne M.K. Buckley, Natalie J. Ward, Jerry K.Y.Chan, Steven J. Howe, Simon N. Waddington
Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 931-945
Author(s): S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki, T. Orii
The Enzymatic Degradation of Heparan Sulfate
Journal: Protein & Peptide Letters
Volume: 24 Issue: 8 Year: 2017 Page: 710-722
Author(s): Laura S. Griffin,Tracey M. Gloster