Search Result "mucopolysaccharidosis type I"
Gene Therapy of Mucopolysaccharidosis Type I Mice: Repeated Administrations and Safety Assessment of pIDUA/Nanoemulsion Complexes
Journal: Current Gene Therapy
Volume: 21 Issue: 5 Year: 2021 Page: 464-471
Author(s): Michelle Fraga,Roselena Silvestri Schuh,Ãdina Poletto,Talita Giacomet de Carvalho,Raqueli Teresinha França,Camila Vieira Pinheiro,Gilherme Baldo,Roberto Giugliani,Helder Ferreira Teixeira,Ursula Matte
Mucopolysaccharidosis Type II (Hunter Syndrome): Clinical Picture and Treatment
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 861-866
Author(s): Michael Beck
Chloramphenicol Enhances IDUA Activity on Fibroblasts from Mucopolysaccharidosis I Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 14 Issue: 2 Year: 2013 Page: 194-198
Author(s): Fabiana Quoos Mayer,Osvaldo Alfonso Artigalas,Valeska Lizzi Lagranha,Guilherme Baldo,Ida Vanessa Schwartz,Ursula Matte,Roberto Giugliani
Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 946-955
Author(s): Patricia I. Dickson, Agnes H. Chen
Therapeutic Options for Mucopolysaccharidosis II (Hunter Disease)
Journal: Current Pharmaceutical Design
Volume: 26 Issue: 40 Year: 2020 Page: 5100-5109
Author(s): Francyne Kubaski,Filippo Vairo,Guilherme Baldo,Fabiano de Oliveira Poswar,Amauri Dalla Corte,Roberto Giugliani
Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 931-945
Author(s): S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki, T. Orii
Recent Advances in Treatment Approaches of Mucopolysaccharidosis VI
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 956-972
Author(s): Roberto Giugliani, Clarissa Gutierrez Carvalho, Silvani Herber, Louise Lapagesse de Camargo Pinto
Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Emerging Treatment Strategies
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 923-930
Author(s): J. de Ruijter, M. J. Valstar, F. A. Wijburg
Effects of Trehalose Administration in Patients withMucopolysaccharidosis Type III
Journal: Current Medicinal Chemistry
Volume: 31 Issue: 20 Year: 2024 Page: 3033-3042
Author(s): Seyed Ahmad Emami,Ali H. Eid
The Significance of Carbohydrate Analyses and the Role of Synthetic substrates in Enzyme Replacement Therapy (ERT) with Special Reference to Mucopolysaccharidosis
Journal: Current Organic Chemistry
Volume: 8 Issue: 6 Year: 2004 Page: 539-555
Author(s): Falguni Dasgupta, R. Irene Masada, Philip L. Alferness, Michael Vellard, William S. Prince